Record mula sa primary source
Inuri ng FDA ang na-update na klinikal na pagsusumite ng pharmacology ng Denali bilang Major Amendment, na nagpalawig ng target na petsa ng aksyon ng PDUFA para sa pinabilis na pag-apruba ng tividenofusp alfa sa MPS II ng tatlong buwan mula Enero 5, 2026 hanggang Abril 5, 2026. Walang bagong data ng bisa, kaligtasan o biomarker na hiniling; ang pagpapalawig ay pamamaraan lamang. Sinabi ng Denali na ang susog ay hindi nagbabago sa klinikal na pharmacology o mga konklusyon ng benepisyo-panganib ng BLA.
EX-99.1 2 ex991pressreleaseq32025.htm EX-99.1 Document Exhibit 99.1 Denali Therapeutics Reports Third Quarter 2025 Financial Results and Business Highlights • Tividenofusp alfa BLA review process for accelerated approval for MPS II continues with productive engagement with the FDA; commercial launch preparations on track • DNL126 Phase 1/2 study enrollment completed, supporting an accelerated approval path in MPS IIIA • Two new regulatory applications submitted to initiate clinical studies with DNL628 (OTV:MAPT) for Alzheimer’s disease and DNL952 (ETV:GAA) for Pompe disease • Tim Van Hauwermeiren, CEO of argenx, to join Denali's Board of Directors • Carole Ho, M.D., Chief Medical Officer, departing company; Peter Chin, M.D., assuming role of Acting CMO and Head of Development • Denali t
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